European Commission follows the MHRA and FDA in granting approval to Casgevy, first gene editing treatment for sickle cell/beta thal! Read more here: https://lnkd.in/e-BZCB-B #genetherapy #sicklecell #Casgevy
About us
We believe the curative potential of gene therapies is enormous, particularly in the battle against rare and genetic diseases. With 350+ clinical trials active and more preclinical innovation underway, there’s a clear opportunity to offer meaningful treatments to patients with significant unmet needs. Our Gene Therapy products help you tackle the most challenging problems, from safety and quality concerns relating to dose and vector type to manufacturing bottlenecks and navigating the evolving regulatory landscape. The mission of the Gene Therapy Event Series is to focus on the most challenging problems facing every aspect of the industry, sourcing leading experts with innovative solutions and distilling this into market-leading conferences. Every event ensures the content you receive and the connections you access will truly give you the insight and inspiration you need to drive the gene therapy community forward.
- Website
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https://hansonwade.com/gene-therapy-conferences/
External link for Gene Therapy Series
- Industry
- Market Research
- Company size
- 201-500 employees
Updates
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"Kyowa Kirin has gained access to Orchard’s portfolio including Libmeldy, a gene therapy approved for metachromatic leukodystrophy (MLD). January 25, 2024" Read more here: https://lnkd.in/e77fUq3D #genetherapy #kyowakirin #orchardtherapeutics
Kyowa Kirin acquires Orchard Therapeutics for $477.6m
pharmaceutical-technology.com
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"US and European regulators could approve up to 17 gene therapies this year, with a top official at the US Food and Drug Administration (FDA) predicting that 2024 will be a “breakout year” in addressing key challenges to developing cell and gene therapies—especially for rare disorders" Read more here: https://lnkd.in/giFqrF7T #genetherapy
FDA, Industry Officials Predict 2024 Will Be 'Breakout Year' for Gene Therapy Approvals - Rare Disease Advisor
https://www.rarediseaseadvisor.com