Researchers are coming up with innovative ways to get massive genes into the right cells – this time, ribozymes come to the rescue. Check out the latest from Nnenna Ohaka at Tides Global below.
An RNA-based technology, StitchR, could be the key to developing effective gene therapies for muscular dystrophies. Read more on Tides Global: https://lnkd.in/e2MmpYBi
An RNA-based technology, StitchR, could be the key to developing effective gene therapies for muscular dystrophies. Read more on Tides Global: https://lnkd.in/e2MmpYBi
Learn from RCA's biotech consultants about Cell and Gene Therapies (ETMPs) & what to look for and adhere to during development. Link Below ↓ https://ow.ly/OUy950TAHHe
Cell and gene therapies can be life-saving treatments, but administering them is a highly complex process. Discover how an Industry Working Group of cell and gene therapy innovators aspires to enhance the patient treatment journey. #DeloitteRippleEffect
Learn the key considerations for developing an efficient upstream AAV production process for in vivo gene therapies. https://sar.to/1fy72 #SimplifyingProgress #InThisTogether #AdvancedTherapies #CellandGeneTherapy
As cell and gene therapies continue to make headlines as a key opportunity for growth, success in this field will require both innovative tech as well as strategic foresight. https://lnkd.in/ggPmre6Z
Unlocking Complex Cell-based Gene Therapies Session 1 presentation by Carl June is starting now. "The Evolution of Cell and Gene Therapies: Current Advances and Challenges." https://lnkd.in/eiVwStgR #CGT
Adeno-Associated Viruses are important tools for therapeutic gene delivery, successfully treating diseases where a gene is missing, required editing or silencing! Our technote on AAV and Gene Therapy discusses the applications of AAV in therapy and its current challenges. BPS Bioscience provides researchers with a set of AAV tools that can support new discoveries. #aav #gene #drusdiscovery https://hubs.ly/Q02FV6yT0
Gene therapies have the potential to greatly improve the lives of patients with rare diseases, but their promise comes with a host of complex challenges. Download our latest white paper to learn how plan sponsors can help drive solutions and propel the future of gene therapies. https://lnkd.in/g6zhhxbw
#DYK that #genetherapies aim to treat the underlying genetic cause of disease by introducing a new gene or editing genes directly? At AGT, we are investigating gene therapies for multiple rare diseases, including #PompeDisease, #FriedreichAtaxia, #MyotonicDystrophy Type 1, and #XLMTM. Learn more about the different approaches to gene therapy, dependent on the condition: https://lnkd.in/gemsEw2c
Learn about today’s top challenges in cell and gene therapy and how to solve them from Ahmed Youssef at this year’s ESACT. Explore more about Sartorius cell and gene therapy solutions: https://sar.to/nsk5p #SimplifyingProgress #InThisTogether #AdvancedTherapies #CellandGeneTherapy #ESACT #ESACT2024
